Status | Study |
Active, not recruiting |
Study Name: Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) Condition: X-linked Severe Combined Immunodeficiency Date: 2010-07-29 Interventions: Genetic: Single infusion of autologous CD34+ cells transduced with the self-inactivating (SIN) gammaretroviral vector pSRS11.EFS.IL2RG.pre |
Recruiting |
Study Name: Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector Condition: Severe Combined Immunodeficiency Date: 2010-05-21 Interventions: Biological: Gene transfer Three procedures: 1) Bone marrow harvest from the patient's posterior iliac cr |
Completed |
Study Name: Newborn Screening for Severe Combined Immunodeficiency (SCID) in a High-Risk Population Condition: Severe Combined Immunodeficiency T Cell Lymphocytopenia Date: 2009-02-17 |
Completed |
Study Name: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID Condition: Severe Combined Immunodeficiency Date: 2008-11-19 Interventions: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Terminated |
Study Name: Treatment for Growth Failure in Patients With X-Linked Severe Combined Immunodeficiency: Phase 2 Study of Insulin-Like Growth Factor-1 Condition: Growth Failure X-linked Severe Combined Immunodeficiency (XSCID Date: 2007-06-21 Interventions: Drug: Increlex |
Completed |
Study Name: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome Condition: Severe Combined Immunodeficiency Date: 2005-09-07 Interventions: Procedure: Stem cell transplant Drug: Filg |
Completed |
Study Name: Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID) Condition: Severe Combined Immunodeficiency Date: 2001-12-17 Interventions: Drug: Gene-Transduced Autologous CD34+ Stem Cells |
Active, not recruiting |
Study Name: Total-Body Irradiation Followed By Cyclosporine and Mycophenolate Mofetil in Treating Patients With Severe Combined Immunodeficiency Undergoing Donor Bone Marrow Transplant Condition: Immune System Disorder Severe Combined Immunodeficiency Date: 2001-01-06 Interventions: Drug: cyclosporine Given PO or |
Completed |
Study Name: Influences on Female Adolescents' Decisions Regarding Testing for Carrier Status of XSCID Condition: Severe Combined Immunodeficiency Date: 2000-10-04 |
Completed |
Study Name: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study Condition: Severe Combined Immunodeficiency Date: 1999-11-03 Interventions: Drug: ADA PBSC Drug: ADA Umbilical Cord Bl |